Pediatric Dermatology Research Alliance (PeDRA) Annual Conference

小儿皮肤病学研究联盟 (PeDRA) 年会

基本信息

批准号：
8986128
负责人：
Anna Lee Bruckner
金额：
$ 3万
依托单位：
UNIVERSITY OF CALIFORNIA, SAN DIEGO
依托单位国家：
美国
项目类别：
财政年份：
2015
资助国家：
美国
起止时间：
2015-09-01 至 2017-08-31
项目状态：
已结题

来源：
https://reporter.nih.gov/project-details/8986128
关键词：
Address Applications Grants Area Basic Science Blood Vessels Case Study Child Child Care Childhood Clinical Clinical Research Clinical Research Protocols Clinical Trials Clinical Trials Design Consensus Consensus Development Cutaneous Dermatologic Dermatologist Dermatology Disease Educational process of instructing Expert Opinion FDA approved Fostering Genetic Genomics Goals Group Meetings Guidelines Health Hereditary Disease Inflammatory Inherited Instruction Knowledge Lesion Life Malignant Neoplasms Measures Methods Modeling Multicenter Studies Natural History Neonatal Outcome Output Patient advocacy Patients Performance Pharmaceutical Preparations Physicians Premature Infant Process Research Research Design Research Infrastructure Research Methodology Research Personnel Research Priority Scientist Skin Staging Strategic Planning Support Groups Systemic Therapy Techniques Technology Therapeutic Therapeutic Intervention Time Translational Research Translations Treatment Protocols Update Vision Vitiligo Work advocacy organizations base clinical care cohort comparative effectiveness data management design drug development effective intervention improved innovation knowledge base lectures malformation meetings novel organizational structure patient advocacy group posters premature prevent public health relevance repository response skills skin disorder symposium therapy outcome tumor working group

项目摘要

DESCRIPTION (provided by applicant): Pediatric dermatologists care for children with a broad range of rare and common disorders, such as severe inflammatory skin diseases that require systemic therapy, disfiguring vascular birthmarks, and genetic skin disorders and cutaneous tumors that can be life-endangering. There is a paucity of FDA-approved therapies for these severe conditions and a great need for standardized treatment protocols and methods to measure response. The Pediatric Dermatology Research Alliance (PeDRA) was established to address this therapeutic shortfall. PeDRA's vision is to create and sustain collaborative research networks that conduct well- designed, high-quality multicenter studies to better understand, prevent, treat and cure dermatologic diseases in children. The PeDRA Annual Conference is central to achieving these goals and includes didactic lectures, interactive discussions led by experts in research methodology, panel and poster sessions, and disease-focused small-group meetings. The specific aims are: 1) To provide new and established PeDRA investigators with an essential knowledge base and infrastructure to conduct high-quality multicenter research in pediatric skin disorders; 2) To identify and prioritize the clinica needs and therapeutic opportunities in five specific areas of pediatric dermatology: inflammatory skin diseases, birthmarks, genetic skin disorders, premature and term neonatal skin, and cutaneous malignancies and precursor lesions; and 3) To enhance opportunities for translational research initiatives and innovative therapeutic approaches by facilitating idea-sharing and dialogue between basic scientists, physician investigators, and clinicians.

描述（由申请人提供）：儿科皮肤科医生护理患有各种罕见和常见疾病的儿童，例如需要全身治疗的严重炎症性皮肤病、毁容的血管胎记以及可能危及生命的遗传性皮肤病和皮肤肿瘤FDA 批准的针对这些严重疾病的治疗方法很少，因此非常需要标准化的治疗方案和测量反应的方法来解决这一问题。 PeDRA 的愿景是建立和维持合作研究网络，开展精心设计的高质量多中心研究，以更好地了解、预防、治疗和治愈儿童皮肤病。 PeDRA 年会是实现这些目标的核心。包括教学讲座、由研究方法专家主导的互动讨论、小组会议和海报会议以及以疾病为重点的小组会议。具体目标是： 1) 为新的和已建立的 PeDRA 研究人员提供必要的知识库和基础设施来开展研究。儿科皮肤病的高质量多中心研究；2) 确定并优先考虑儿科皮肤病学五个特定领域的临床需求和治疗机会：炎症性皮肤病、胎记、遗传性皮肤病、早产儿和足月新生儿皮肤病以及皮肤恶性肿瘤和3) 通过促进基础科学家、医师研究人员和超级明星之间的思想共享和对话，增加转化研究计划和创新治疗方法的机会。