CLINICAL TRIAL: MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE

临床试验：MYOZYME 治疗晚发性庞贝病患者

• 批准号: 7724952
• 负责人: BRUCE A BARSHOP
• 金额: $ 1.1万
• 依托单位: UNIVERSITY OF CALIFORNIA, SAN DIEGO
• 依托单位国家: 美国
• 财政年份: 2007
• 资助国家: 美国
• 起止时间: 2007-12-01 至 2008-11-30
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7724952
• 关键词: Clinical Trials; Computer Retrieval of Information on Scientific Projects Database; Funding; Glycogen storage disease type II; Grant; Institution; Patients; Placebos; Research; Research Personnel; Resources; Safety; Source; United States National Institutes of Health

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. Evaluate the safety, efficacy and PK of Myozyme treatment in patients with late onset Pompe disease compared to placebo.

该副本是利用众多研究子项目之一 由NIH/NCRR资助的中心赠款提供的资源。子弹和 调查员（PI）可能已经从其他NIH来源获得了主要资金， 因此可以在其他清晰的条目中代表。列出的机构是 对于中心，这不一定是调查员的机构。 与安慰剂相比，评估肌酶治疗的安全性，功效和PK的安全性和PK。