CLINICAL TRIAL: EXTENSION STUDY - LATE ONSET POMPE DISEASE

临床试验：扩展研究 - 迟发性庞贝病

• 批准号: 7950980
• 负责人: BRUCE A BARSHOP
• 金额: $ 0.68万
• 依托单位: UNIVERSITY OF CALIFORNIA, SAN DIEGO
• 依托单位国家: 美国
• 财政年份: 2008
• 资助国家: 美国
• 起止时间: 2008-12-01 至 2009-11-30
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7950980
• 关键词: Clinical Research; Clinical Trials; Computer Retrieval of Information on Scientific Projects Database; Double-Blind Method; Funding; Glycogen storage disease type II; Grant; Institution; Orphan Disease; Patients; Placebo Control; Research; Research Personnel; Resources; Safety; Source; United States National Institutes of Health

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. Assess the long term safety and efficacy of Myozyme treatment in patients with late onset Pompe disease who were previously treated under the placebo-controlled, double blind study AGLU02704. Orphan disease status.

该副本是利用众多研究子项目之一 由NIH/NCRR资助的中心赠款提供的资源。子弹和 调查员（PI）可能已经从其他NIH来源获得了主要资金， 因此可以在其他清晰的条目中代表。列出的机构是 对于中心，这不一定是调查员的机构。 评估肌酶治疗对迟发性蓬松疾病患者的长期安全性和功效，这些患者以前在安慰剂对照的，双盲研究AGLU02704下进行了治疗。 孤儿疾病状况。