Administrative Core - Novel Therapeutics for FSHD

行政核心 - FSHD 的新疗法

• 批准号: 10197167
• 负责人: CHARLES P. EMERSON
• 金额: $ 10.8万
• 依托单位: UNIV OF MASSACHUSETTS MED SCH WORCESTER
• 依托单位国家: 美国
• 财政年份: 2008
• 资助国家: 美国
• 起止时间: 2008-09-10 至 2023-05-31
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/10197167
• 关键词: Administrator; Advisory Committees; Biomaterials Research; Boston; Businesses; Cell Line; Child; Clinical; Clinical Management; Collaborations; Communication; Communities; Community Outreach; Contracts; Core Facility; Development; Environment; Facioscapulohumeral Muscular Dystrophy; Feedback; Funding; Goals; Human Resources; Industry; Institution; International; Internet; Leadership; Massachusetts; Mission; Muscle Cells; Muscular Dystrophies; Pathogenesis; Patients; Policies; Procedures; Records; Reporting; Research; Research Personnel; Research Project Grants; Research Training; Resource Sharing; Resources; Schedule; Scientist; Societies; Training; Training and Education; United States National Institutes of Health; Universities; Work; cell repository; data sharing; drug development; experience; industry partner; medical schools; meetings; novel therapeutics; outreach; patient advocacy group; patient outreach; programs; symposium; web site; working group

PROJECT SUMMARY The Administrative Core A will be responsible for the planning, development, coordination, and overall administration of the University of Massachusetts Medical School (UMMS) W ellstone MD CRC focused on Facioscapulohumeral Muscular Dystrophy (FSHD). Center leadership will continue under Dr. Charles Emerson at UMMS, Dr. Louis Kunkel at Children's Boston, and Kathryn Wagner at Kennedy Krieger, all highly experienced research administrators and accomplished scientists. The administrative unit for Core A will be located at UMMS, which has substantial resources, personnel and experience for management of a P50 Center. Core A will be the administrative hub to manage all Center resources and communications and carry out policies and procedures that establish an energized environment to enable effective communication and collaboration among all the Center constituents, including investigators, trainees, FSHD patients and advocacy groups, industry partners, NIH and the public. The Center will promote its mission through its website, which disseminates information on Center activities, biomaterials and research, and through its partnership with patient advocacy groups, particularly the FSH Society, which co-sponsors FSHD Research W orkshops and Researcher-Patient Networking meetings to engage patients, researchers, trainees and NIH in our Center mission. Through Core A, the Center will promote the distribution of muscle cell lines from its W ellstone FSHD Cell Repository as a unique FSHD bio-resource. Internal committees will enable Center leadership, investigators and trainees to effectively utilize resources, organize internal dataflow and communications, and receive feedback on Center management, research progress and training. Regularly- scheduled web conference meetings will focus on trainee and PI data sharing and research planning, and an annual W ellstone Center Retreat at UMMS will bring investigators and trainees face-to-face with a Center Advisory Committee (CAC) and NIH program leaders to review research progress, set goals and align Center activities with the NIH W ellstone Center Network.

项目摘要 行政核心A将负责计划，开发，协调和整体 马萨诸塞大学医学院（UMMS）的管理W Ellstone MD CRC专注于 Facioscapulohumeral肌肉营养不良（FSHD）。在查尔斯博士的领导下，中心领导将继续 艾姆森（Emerson）在Umms，波士顿儿童的路易斯·昆克尔（Louis Kunkel）和肯尼迪·克里格（Kennedy Krieger）的凯瑟琳·瓦格纳 经验丰富的研究管理员和有成就的科学家。核心A的管理单位 将位于UMMS，具有大量资源，人员和经验，用于管理 P50中心。核心A将是管理所有中心资源和通信的行政枢纽， 执行建立充满活力的环境以实现有效沟通的政策和程序 以及所有中心选民之间的合作，包括调查人员，学员，FSHD患者和 倡导团体，行业合作伙伴，NIH和公众。该中心将通过其使命来促进其使命 网站，该网站传播有关中心活动，生物材料和研究的信息，并通过其中心活动 与患者倡导小组的合作伙伴关系，尤其是FSH协会，该协会共同赞助FSHD研究 W Orkshops和研究人员与患者网络会议，以吸引患者，研究人员，受训者和NIH 在我们的中心任务中。通过核心A，该中心将促进肌肉细胞系的分布 W Ellstone FSHD细胞存储库是独特的FSHD生物资源。内部委员会将启用中心 领导，调查人员和受训者有效利用资源，组织内部数据流和 沟通，并收到有关中心管理，研究进度和培训的反馈。经常- 预定的网络会议会议将重点关注受训者和PI数据共享和研究计划，以及 UMMS的年度W Ellstone Center Retreat将与中心面对面的调查人员和学员面对面 咨询委员会（CAC）和NIH计划负责人审查研究进度，设定目标和对齐中心 NIH W Ellstone Center网络的活动。