CLINICAL TRIAL: GAUCHER REGISTRY

临床试验：Gaucher 注册中心

• 批准号: 7719114
• 负责人: ROBERT A GREENSTEIN
• 金额: $ 0.16万
• 依托单位: UNIVERSITY OF CONNECTICUT SCH OF MED/DNT
• 依托单位国家: 美国
• 财政年份: 2008
• 资助国家: 美国
• 起止时间: 2008-04-01 至 2009-03-31
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7719114
• 关键词: Clinical; Clinical Trials; Computer Retrieval of Information on Scientific Projects Database; Condition; Data; Databases; Funding; Gaucher Disease; Grant; Institution; International; Natural History; Outcome; Patients; Pattern; Physicians; Registries; Research; Research Personnel; Resources; Source; United States National Institutes of Health; enzyme replacement therapy; member; post-market; response

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. The Gaucher Registry is an ongoing, post-marketing, observational database that tracks outcomes of routine clinical practice for patients with Gaucher disease. Not all patients in the Registry are on Enzyme Replacement Therapy (ERT). All physicians participating in the Registry are considered members of the International Collaborative Gaucher Group (ICGG). Data collected from ICGG physicians will represent Gaucher disease practice patterns under common clinical conditions. Thus, the data collected by this international, collaborative Registry will provide information to better characterize the natural history and progression of Gaucher disease, as well as the clinical responses of patients whose physicians have prescribed ERT.

该副本是利用众多研究子项目之一 由NIH/NCRR资助的中心赠款提供的资源。子弹和 调查员（PI）可能已经从其他NIH来源获得了主要资金， 因此，可以在其他清晰的条目中表示。列出的机构是 对于中心，这不一定是调查员的机构。 Gaucher注册表是一个持续的，销售后的观察数据库，可跟踪Gaucher病患者常规临床实践的结果。并非所有注册表中的患者均进行酶替代疗法（ERT）。所有参加注册表的医生都被视为国际合作Gaucher集团（ICGG）的成员。 从ICGG医生那里收集的数据将代表常见临床状况下的Gaucher病练习模式。 因此，该国际协作注册中心收集的数据将提供信息，以更好地表征Gaucher病的自然病史和进展，以及医生开出ERT的患者的临床反应。