Pediatric Dermatology Research Alliance Annual Conference

小儿皮肤病学研究联盟年会

基本信息

批准号：
8597492
负责人：
KEITH A CHOATE
金额：
$ 5.96万
依托单位：
MEDICAL COLLEGE OF WISCONSIN
依托单位国家：
美国
项目类别：
财政年份：
2013
资助国家：
美国
起止时间：
2013-09-01 至 2015-08-31
项目状态：
已结题

来源：
https://reporter.nih.gov/project-details/8597492
关键词：
Address Advocacy Applications Grants Area Basic Science Blood Vessels Case Study Child Child Care Childhood Clinical Clinical Research Clinical Research Protocols Clinical Sciences Clinical Trials Commit Consensus Development Data Analyses Dermatologic Dermatologist Dermatology Disease Educational process of instructing Epidermolysis Bullosa Expert Opinion FDA approved Fostering Genetic Goals Group Meetings Guidelines Health Hemangioma Individual Inflammatory Inherited Institutional Review Boards Life Measures Methods Mission Multicenter Studies Outcome Outcome Measure Participant Patients Pharmaceutical Preparations Pilot Projects Population Recruitment Activity Research Research Design Research Infrastructure Research Methodology Research Personnel Scientist Support Groups Systemic Therapy Talents Therapeutic Therapeutic Intervention Time Training Translational Research Translations Treatment Protocols Vision Writing advocacy organizations clinical care design improved keratinization knowledge base lectures meetings posters prevent public health relevance research study response skin disorder symposium working group

项目摘要

DESCRIPTION (provided by applicant): Pediatric dermatologists care for children with a broad range of rare and common disorders, such as severe inflammatory skin diseases that require systemic therapy, disfiguring vascular birthmarks, and genetic skin disorders that can be life-endangering. There is a paucity of FDA-approved therapies for these severe conditions and a great need for standardized treatment protocols and methods to measure response to therapy. The Pediatric Dermatology Research Alliance (PeDRA) was established to address this therapeutic shortfall. PeDRA's vision is to create and sustain collaborative research networks that conduct well-designed, high-quality multicenter studies to better understand, prevent, treat and cure dermatologic diseases in children. The PeDRA Annual Conference is central to achieving these goals and will include didactic lectures, interactive discussions led by experts in research methodology, poster sessions, and disease-focused small-group meetings. The specific aims are: 1) To provide new and established PeDRA investigators with an essential knowledge base and infrastructure to conduct high-quality multicenter research in pediatric skin disorders; 2) To create a bridge between basic scientists and clinicians to enhance opportunities for translational research initiatives; and 3) To identify and prioritize the clinical needs and therapeutic opportunities in four disease- specific areas: inflammatory skin diseases, hemangiomas, epidermolysis bullosa, and disorders of keratinization. An additional goal is to expand the research mission beyond the established working groups to other disorders with need.

描述（由申请人提供）：小儿皮肤科医生护理各种罕见和常见疾病的儿童，例如需要全身治疗的严重炎症性皮肤病，毁容血管胎记和遗传性皮肤疾病，这些疾病可能会成为生命。对于这些严重疾病，FDA批准的疗法很少，并且非常需要标准化治疗方案和测量对治疗反应的方法。建立了儿科皮肤病学研究联盟（PEDRA），以解决这种治疗性短缺。佩德拉（Pedra）的愿景是创建和维持协作研究网络，以进行精心设计，高质量的多中心研究，以更好地理解，预防，治疗，治愈儿童的皮肤病学疾病。 PEDRA年度会议对于实现这些目标至关重要，并将包括教学演讲，由专家的专家主持的互动讨论研究方法，海报会议和以疾病为中心的小组会议。具体目的是：1）为新的且已建立的PEDRA研究人员提供基本的知识库和基础设施，以在小儿皮肤疾病中进行高质量的多中心研究； 2）在基本科学家和临床医生之间建立桥梁，以增强转化研究计划的机会； 3）在四个疾病的领域中识别和确定临床需求和治疗机会：炎症性皮肤疾病，血管瘤，表皮溶液bull和角质化疾病。另一个目标是将研究任务扩展到有需要的其他疾病之外。